Starting iron chelation therapy early may prevent growth problems and organ damage from iron overload in children with TDT. Currently approved medications have limitations for use in very young ...
Mitapivat is the first FDA-approved oral therapy for anaemia in all forms of thalassemia Reduced transfusion dependence may ...
A groundbreaking oral treatment for thalassemia, Mitapivat, has received US FDA approval, offering hope for adults with this ...
Patients on dopaminergic agonists (n, mean daily L-dopa equivalent in mg) 18 (243) 18 (220) 4 (225) 13 (250) Patients on L-dopa and agonists (n) 7 7 2 5 Cognition and behavior: MDS-UPDRS part I score ...
Transfusion-dependent β-thalassemia (TDT) patients in France face significant health care demands and clinical challenges, with frequent complications and high mortality rates. Patients with TDT ...
An iron-binding drug that is already approved for treatment of other diseases could provide a novel way to attack ovarian tumors, according to a new study led by Weill Cornell Medicine researchers.
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